Cure Rare Disease develops life-saving treatments for children impacted by fatal rare diseases.
Through collaborations with world-renowned academics and clinicians, we are moving science forward to develop life-saving gene therapies for rare and ultra-rare disease patients overlooked and underserved by traditional drug development efforts.
Dollars invested into R&D
$3.5M
Potential lives impacted
200,000+
Number of drugs in development
19
Number of clinical trials
1
All Proceeds Raised Help to Save:
Terry H.
Terry, 27, works in computer technology, and has always been passionate about gaming. Terry has Duchenne muscular dystrophy, and was the catalyst behind Cure Rare Disease.
Fritz K.
Fritz, 7, was diagnosed with Duchenne muscular dystrophy in 2017. He lives with his family in AZ and wants to be a scientist when he grows up!
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